Trial Basics
1 / 19
Introducing Courageous Parents Network's new unit EVALUATING THE CLINICAL TRIAL OPTION
Clinical Trials: In the early phase, it’s about both gaining knowledge and trying to help. To figure it out, we need some families to step up and go first
Everyone who participates in rare disease research is a medical hero
Clinical Trials: Phase 1 defined – focusing on safety, with less certainty about benefit. Phase 1 trials for rare disease are designed for some efficacy
